The Division of Genetics, Department of Pediatrics at the All India Institute of Medical Sciences (AIIMS), New Delhi, has announced the launch of a significant interventional clinical trial: ELEGANT. Read More
A new Phase 3 study, titled NAVIGATE, is currently evaluating the efficacy and safety of Nizubaglustat for patients with late-infantile and juvenile forms of Niemann-Pick Type C (NPC) and GM1/GM2 Gangliosidosis. Read More